Propionic Acidemia Therapeutic Market is driven by Gene Therapy Advancements
Propionic acidemia is a rare, inherited metabolic disorder characterized by a deficiency of the propionyl-CoA carboxylase enzyme, leading to toxic metabolite buildup. Therapeutic solutions in this market range from dietary management products and amino acid formulae to innovative enzyme replacement and gene therapy candidates. These products aim to reduce propionate accumulation, stabilize...
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